We are delighted to add our latest Educational Series on spinal muscular atrophy. This review article includes details on the burden and treatments available for SMA, disease modifying therapies and clinical studies on the long-term treatment with nusinersen.
The review includes guiding commentary from Professor Monique Ryan, Director of the Neurology Department of the Royal Children’s Hospital, Melbourne Australia, where she is also head of the neuromuscular clinical research program and multidisciplinary Neuromuscular Clinic.
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